Gaucher Disease Drugs Market

Global Gaucher Disease Drugs Market Size, Share And Trend Analysis Report By Type (Type 1 GD, Type 2, Type 3, Others), By Therapy (Enzyme Replacement Therapy, Substrate Replacement Therapy) Forecast (2021-2027)
    Update Available - Forecast 2024-2030   

Published: Jul 2023 | Report Code: OMR2025286 | Category : Pharmaceuticals | Delivery Format: /

The global gaucher disease drugs market is expected to grow at a significant CAGR during the forecast period (2021-2027). Gaucher disease is an autosomal recessive metabolic illness that affects one in every 100,000 people. The most prevalent lysosomal storage disorder is this one. Mutations in the GBA gene induce a decrease in the synthesis of glucocerebrosidase and, as a result, a buildup of glucocerebroside. Excess lipid builds up in the brain, bone marrow, lungs, kidney, liver, and spleen, interfering with normal physiological functions.

During the forecast period, the market is expected to increase at a moderate pace. One of the key growth boosters for the market is the rising frequency of the condition and increased efforts to identify more GD patients. The lack of late-stage pipeline medications and escalating treatment costs are preventing the market from reaching its full potential. The development of new medicines that combat neuronopathic consequences at lower costs and with more flexible administration schedules remains a significant unmet need. Increasing investments in research and development efforts connected to rare diseases, on the other hand, are expected to affect the market's future.

Owing to robust sales of Cerezyme and Cerdelga, the company will maintain its global significance in the next years. Elelyso from Pfizer competes fiercely with Vpriv from the Shire; both enzyme replacement medications are used to treat GD type 1. Elelyso was denied regulatory approval in Europe, where Vpriv has held a ten-year commercial monopoly since 2010. Collaborations for the development and marketing of treatments drive the market. 

Market Coverage

  • The market number available for – 2020-2027
  • Base year- 2020
  • Forecast period- 2021-2027
  • Segment Covered
  • Regions Covered- Globally

Competitive Landscape: Sanofi Genzyme, Shire, Pfizer, and Johnson & Johnson. Sanofi Genzyme among others. 

Key questions addressed by the report

  • What is the market growth rate?
  • Which segment and region dominates the market in base year?
  • Which segment and region will project fastest growth in the market?
  • How COVID-19 impacted the market?

o Recovery Timeline

o Deviation from pre-COVID forecast

o Most affected region and segment

  • Who is the leader in the market?
  • How players are addressing challenges to sustain growth?
  • Where is the investment opportunity?

Global Gaucher Disease Drugs Market by Segments

By Type

Type 1 GD

Type 2

Type 3

Others 

By Therapy 

Enzyme Replacement Therapy

Substrate Replacement Therapy 

Global Gaucher Disease Drugs Market by Region

North America

  • United States
  • Canada

Europe

  • UK
  • Germany
  • Italy
  • Spain
  • France
  • Rest of Europe 

Asia-Pacific

  • China
  • India
  • Japan
  • South Korea
  • Rest of Asia-Pacific 

Rest of the World